Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth. Scientists at St. Jude Children’s Research Hospital led the first in uterotreatment of SMA with the orally administered drug risdiplam.
First prenatal treatment for spinal muscular atrophy shows promising results
- Post author:admin
- Post published:February 20, 2025
- Post category:uncategorized